Development of potent monoclonal antibody auristatin conjugates for cancer therapy

SO Doronina, BE Toki, MY Torgov… - Nature …, 2003 - nature.com
SO Doronina, BE Toki, MY Torgov, BA Mendelsohn, CG Cerveny, DF Chace, RL DeBlanc…
Nature biotechnology, 2003nature.com
We describe the in vitro and in vivo properties of monoclonal antibody (mAb)-drug
conjugates consisting of the potent synthetic dolastatin 10 analogs auristatin E (AE) and
monomethylauristatin E (MMAE), linked to the chimeric mAbs cBR96 (specific to Lewis Y on
carcinomas) and cAC10 (specific to CD30 on hematological malignancies). The linkers used
for conjugate formation included an acid-labile hydrazone and protease-sensitive
dipeptides, leading to uniformly substituted conjugates that efficiently released active drug in …
Abstract
We describe the in vitro and in vivo properties of monoclonal antibody (mAb)-drug conjugates consisting of the potent synthetic dolastatin 10 analogs auristatin E (AE) and monomethylauristatin E (MMAE), linked to the chimeric mAbs cBR96 (specific to Lewis Y on carcinomas) and cAC10 (specific to CD30 on hematological malignancies). The linkers used for conjugate formation included an acid-labile hydrazone and protease-sensitive dipeptides, leading to uniformly substituted conjugates that efficiently released active drug in the lysosomes of antigen-positive (Ag+) tumor cells. The peptide-linked mAb-valine-citrulline-MMAE and mAb-phenylalanine-lysine-MMAE conjugates were much more stable in buffers and plasma than the conjugates of mAb and the hydrazone of 5-benzoylvaleric acid-AE ester (AEVB). As a result, the mAb-Val-Cit-MMAE conjugates exhibited greater in vitro specificity and lower in vivo toxicity than corresponding hydrazone conjugates. In vivo studies demonstrated that the peptide-linked conjugates induced regressions and cures of established tumor xenografts with therapeutic indices as high as 60-fold. These conjugates illustrate the importance of linker technology, drug potency and conjugation methodology in developing safe and efficacious mAb-drug conjugates for cancer therapy.
nature.com